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Regulatory-Compliant Validation of a Highly Sensitive qPCR for Biodistribution Assessment of Hemophilia A Patient Cells. Bittorf P, Bergmann T, Merlin S, Olgasi C, Pullig O, Sanzenbacher R, Zierau M, Walles H, Follenzi A, Braspenning J. Mol Ther Methods Clin Dev. 2020 Jun 1;18:176-188. doi: 10.1016/j.omtm.2020.05.029. eCollection 2020 Sep 11.
Combined ATMPs Containing Genetically Modified Cells. Bittorf P, Zierau M, Sanzenbacher R, Walles H, Braspenning J. pharmazeutische medizin, 2017, 19 (3): 168-174